Categories
Health

FDA Advisors Mostly Convinced Arimoclomol Works for Rare Genetic Disorder

Source link : https://www.newshealth.biz/health-news/fda-advisors-mostly-convinced-arimoclomol-works-for-rare-genetic-disorder/

A majority of FDA committee advisors were on the same page regarding the efficacy of an investigative treatment for an ultra-rare and fatal neurovisceral genetic disorder, but some still had concerns. In an 11-5 vote Friday, the Genetic Metabolic Diseases Advisory Committee said the totality of clinical, nonclinical data, and favorable safety profile underpinning arimoclomol […]

Author : News Health

Publish date : 2024-08-03 16:23:18

Copyright for syndicated content belongs to the linked Source.

................................*...........................................++++++++++++++++++++--------------------.....