Source link : https://www.newshealth.biz/health-news/fda-panel-to-consider-arimoclomol-for-rare-genetic-disorder/
An FDA advisory committee meeting this week will focus on whether an investigative treatment for an ultra-rare and fatal neurovisceral genetic disorder is truly efficacious. On Friday, the Genetic Metabolic Diseases Advisory Committee will vote on whether the data supporting arimoclomol shows efficacy for adults and children ages 2 years and older with Niemann-Pick disease […]
Author : News Health
Publish date : 2024-08-01 15:16:02
Copyright for syndicated content belongs to the linked Source.
Categories