Source link : https://www.newshealth.biz/health-news/second-drug-okd-for-ultra-rare-neurodegenerative-disease/
The FDA gave the green light to levacetylleucine (Aqneursa) as a stand-alone treatment for Niemann-Pick disease type C (NPC), just days after approving the first drug for the ultra-rare genetic disease. The oral suspension therapy is a modified amino acid indicated to treat neurological manifestations of NPC in adults and pediatric patients who weigh at […]
Author : News Health
Publish date : 2024-09-25 17:30:04
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